September 2024 | Journal Articles

Human T cell generation is restored in CD3δ severe combined immunodeficiency through adenine base editing

Authors: Gelfer, Wu, Romero, Christian, Kohn, Chang, H., X., Z., V., DB, PC, Seet, Kang, Wright, Wong, Newby, GA, CS, S-H L, N., RL, Campo-Fernandez, Narendran, Garibay, Liu, McAuley, Everette, B., A., A., DR, GE, KA, Fitz-Gibbon, Murguia-Favela, Butler, Crooks, Yiu, Azzun, ST, L., J., GM, G., A.

Published: Cell, 2023:186:7, 1398-1416

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